The NHS will offer a long-acting antibody injection to protect thousands of premature and vulnerable babies from respiratory syncytial virus (RSV) starting this autumn.
The NHS will provide a new triple combination therapy to hundreds of children and adults with cystic fibrosis in England, aiming to improve lung function and quality of life for eligible patients.
A first-in-patient trial using AAV-based OTOF gene therapy, led by Karolinska Institutet and Chinese hospitals, restored hearing (improving from 106 dB to 52 dB) in 10 individuals aged 1–24.
A Stanford-led phase 3 trial shows gene therapy skin grafts significantly heal chronic wounds in patients with severe epidermolysis bullosa, reducing pain and improving quality of life.
Around 20,000 children and young people with type 1 diabetes in England now benefit from life-changing 'artificial pancreas' technology, recommended by NICE.
There is a beacon of hope for patients with a rare genetic disorder called Werner Syndrome as researchers unveil a groundbreaking discovery: Nicotinamide riboside, a vitamin B3 derivative, reverses premature ageing.
Having a pet dog may lower the risk of eczema in children who are genetically prone to the condition, shedding light on how environmental factors may influence genetic risks.
The National Institute for Health and Care Research Great Ormond Street Hospital Biomedical Research Centre is developing a new virtual reality (VR) game to help children rehabilitate after brain tumour treatment.
Expectant mothers are set to receive safer maternity care as the NHS prepares to roll out a new programme aimed at preventing brain injuries in childbirth.
