gene therapy - search results

Pascale V Guillot from University College London, Elizabeth Garrett Anderson Institute for Women’s Health, explains stem cell and gene therapy to treat osteogenesis imperfecta, but is this hype or hope?

Dr Jen Vanderhoven, Director, National Horizons Centre, Teesside University, sheds some light on how the gene therapy field can progress in the face of funding challenges and skills shortages.

Scientists in France have partially restored the eyesight of a blind man, using gene therapy - he is now able to identify blurry shapes.

Scientists from Trinity College Dublin have developed a new gene therapy for an eye disease that leads to progressive loss of vision.

Lalit Singh Pukhrambam, PhD, and Ahmed S Ibrahim, PhD from Wayne State University School of Medicine in the U.S. focus here on the importance of combating diabetic retinopathy.

Dr. Arun Srivastava, George H. Kitzman Professor of Genetics, from the University of Florida describes the rationale and strategies for the development of next generation (NextGen), generation X (GenX) and optimised (Opt) recombinant AAV vectors for human gene therapy Recombinant AAV vectors have been, or are currently being, used in...

Kapil Bharti, PhD, Senior Investigator and Head of the Ocular and Stem Cell Translational Research Section at the National Eye Institute (NEI), explains testing the safety of a stem cell therapy for age-related macular degeneration in this special focus on eye health.

Laura Hagerty, PhD, Scientific Portfolio Director at the Muscular Dystrophy Association, highlights strategies for gene correction to treat Duchenne muscular dystrophy.

Dr Takashi Nakamura from Hokkaido University challenges the potential of nano-tech based drug delivery system (Nano DDS) in the development of next-generation cancer immunotherapy.

Discovering cures for human diseases or how to recover from damage or trauma to tissues is the fundamental goal of medical researchers, but it is a daunting task. Nevertheless, recent studies have shown the remarkable potential of the spiny mouse in addressing these crucial issues

The fascinating research of Professor Brunhilde Wirth is placed under the spotlight, concerning her work in the field of disease-causing genes, modifier pathways and pathomechanisms of neuromuscular disorders, focussing on spinal muscular atrophy (SMA)

Prof Dr. Michael Roth, University Hospital Basel looks at how asthma therapy can reduce the effects of airway wall remodelling

Stefaan Van Gool, MD, PhD brings to light the important role of Individualised Multimodal Immunotherapy in improving the survival of brain cancer.

CEO of Brittle Bone Society Patricia Osborne, revisits aspects of the condition and shares what is known around current medical research and treatments, speaking to experts attached to the Charity.

Prof Dr Susanne M Bailer, Fraunhofer Institute for Interfacial Engineering and Biotechnology IGB, explains the possibilities of an oncolytic virus platform technology.

Pascale V Guillot, Associate Professor at University College London, investigates the possibility of exosome therapy for those living with brittle bone disease.

Here, Professor of Biochemistry, Microbiology & Immunology at the University of Saskatchewan, Peter Betscher, explains how he is dedicated towards realising Robert North’s vision.

New research suggests that in suppressing a mutated ALS gene, it may be possible to delay to onset of symptoms.

Sean E. Lawler PhD from Brown University Cancer Center, an experienced scientist in the brain tumour field

Professor Olivier Braissant, believes there is hope for the treatment of creatine deficiency thanks to new genetic disease research - here, he tells us all about the recent developments.