Rare Diseases

Scientists find way to reverse nerve damage in rare ALS form

Researchers using patient-derived stem cells reveal a rare ALS mutation triggers a chronic stress response in motor neurons, blocking it reverses damage in lab models, paving the way for new treatment strategies.

Modern research into rare diseases

Research infrastructure project manager at EURORDIS, Virginie Bros-Facer highlights the extent of rare diseases in Europe in this insightful article

Health officials pledge to reduce cholera deaths by 90%

Health Officials from across the globe are set to meet in France and pledge to dramatically reduce cholera deaths by 2030

The impact of clinical research in rare diseases

Kit C.B. Roes from the University Medical Centre, Utrecht outlines why clinical research in rare diseases requires swift implementation of new methodology

The European Confederation of Pharmaceutical Entrepreneurs AISBL

The European Confederation of Pharmaceutical Entrepreneurs (EUCOPE) is Europe’s principal trade body for small to medium-sized innovative companies working in the field of pharmaceuticals....

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Latest Academic Articles

The latest academic articles from key research stakeholders