Researchers using patient-derived stem cells reveal a rare ALS mutation triggers a chronic stress response in motor neurons, blocking it reverses damage in lab models, paving the way for new treatment strategies.
Kit C.B. Roes from the University Medical Centre, Utrecht outlines why clinical research in rare diseases requires swift implementation of new methodology
The European Confederation of Pharmaceutical Entrepreneurs (EUCOPE) is Europe’s principal trade body for small to medium-sized innovative companies working in the field of pharmaceuticals....
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